This is fantastic news!
The FDA has just approved a Vertex drug called Kalydeco, which is the first drug aimed at treating the underlying cause of Cystic Fibrosis, which is a genetic disease.
The sad news is that Kalydeco aims to treat a protein that causes CF in only about 4% of cases… but this is a huge step because they're testing Kalydeco in conjunction with other treatments that aim to take on 90% of CF patients!!
Right now, CF affects about 30k of people in the U.S. alone.
With all this good news, we were hoping that it wouldn't be absurdly expensive — and at the required two pill a day, it still seems terribly steep: $294,000 a year!
ARE YOU KIDDING US? You really can't do any better than that when you're in the business of helping people??
The worst part is that they know they can charge that because people need it.
Either way, we're glad there's something now. We just hope they get some competition soon to bring that price down.
[Image via AP Images.]